FDA approves two gene therapies for sickle cell disease, including first that uses CRISPR/Cas9
goodai.substack.com
These approvals represent an important medical advance with the use of innovative cell-based gene therapies to target potentially devastating diseases and improve public health, Today’s actions follow rigorous evaluations of the scientific and clinical data needed to support approval, reflecting the FDA’s commitment to facilitating the development of safe and effective treatments for conditions with severe impacts on human health.
FDA approves two gene therapies for sickle cell disease, including first that uses CRISPR/Cas9
FDA approves two gene therapies for sickle…
FDA approves two gene therapies for sickle cell disease, including first that uses CRISPR/Cas9
These approvals represent an important medical advance with the use of innovative cell-based gene therapies to target potentially devastating diseases and improve public health, Today’s actions follow rigorous evaluations of the scientific and clinical data needed to support approval, reflecting the FDA’s commitment to facilitating the development of safe and effective treatments for conditions with severe impacts on human health.